KEGG DRUG: Eladocagene exuparvovec

DRUG: Eladocagene exuparvovec

Entry

D12407                      Drug

Name

Eladocagene exuparvovec (USAN/INN);
Eladocagene exuparvovec-tneq;
Kebilidi (TN);
Upstaza (TN)

Product

KEBILIDI (PTC Therapeutics)

Remark

ATC code:

A16AB26

Product:

D12407<US>

Efficacy

Nervous system disease agent

Disease

Aromatic L-amino acid decarboxylase deficiency [DS:H01161]

Type

Gene therapy product

Comment

Recombinant AAV2 vector containing the human cDNA for the DDC geneTreatment of AADC deficiency

Target

DDC* [HSA_VAR:1644v1] [HSA:1644] [KO:K01593]

Pathway

hsa00350

Tyrosine metabolism

hsa00380

Tryptophan metabolism

Network

nt06028

Dopamine and serotonin metabolism

Brite

Anatomical Therapeutic Chemical (ATC) classification [BR:br08303]
A ALIMENTARY TRACT AND METABOLISM
  A16 OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
   A16A OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
    A16AB Enzymes
     A16AB26 Eladocagene exuparvovec
      D12407  Eladocagene exuparvovec (USAN/INN) <US>
Target-based classification of drugs [BR:br08310]
Enzymes
  Lyases (EC4)
   Carboxy-lyases
    DDC* [HSA_VAR:1644v1]
     D12407  Eladocagene exuparvovec (USAN/INN) <US>
New drug approvals in the USA [br08319.html]
Cellular and gene therapy products
  D12407
New drug approvals in Europe [br08329.html]
European public assessment reports (EPAR) authorised medicine
  D12407
Cellular and gene therapy products
  D12407
New drug approvals in the USA, Europe and Japan [br08328.html]
Approval dates by FDA, EMA and PMDA
  D12407
Pharmacogenomic biomarkers [br08341.html]
Germline mutations in genetic disorder treatments
  D12407

Other DBs

CAS:	2098615-91-7

PubChem:

497620820

LinkDB

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